Gene Therapy - National Human Genome Research Institute
Gene therapy is a technique that uses a gene (s) to treat, prevent or cure a disease or medical disorder. Often, gene therapy works by adding new copies of a gene that is broken, or by replacing a defective or missing gene in a patient’s cells with a healthy version of that gene.

Gene Therapy - Nature
At the forefront of medicine, Gene Therapy brings you the latest research into genetic and cell-based technologies to treat disease.

What Is Gene Therapy? Pros, Cons & Examples - Cleveland Clinic
What is gene therapy? Gene therapy is a type of treatment for genetic disorders. It works by either changing a disease-causing gene or giving you a working copy of that gene. Genes are instructions for making proteins that help your body work.

Gene therapy - Wikipedia
Gene therapy is medical technology that aims to produce a therapeutic effect through the manipulation of gene expression or through altering the biological properties of living cells. [1][2][3][4]

Gene therapy - Mayo Clinic
Gene therapy aims to fix a faulty gene or replace it with a healthy gene to try to cure disease or make the body better able to fight disease. It holds promise as a treatment for a wide range of diseases, such as cancer, cystic fibrosis, heart disease, diabetes, hemophilia and AIDS.

Gene Therapy | New England Journal of Medicine
The goal of gene therapy for genetic diseases is to achieve durable expression of the therapeutic gene or “transgene” at a level sufficient to ameliorate or cure disease symptoms with minimal...

Gene therapy | Description, Uses, Examples, & Safety Issues - Britannica
Gene therapy, introduction of a normal gene into an individual’s genome in order to repair a mutation that causes a genetic disease. Human gene therapy has been attempted on somatic (body) cells for diseases such as cystic fibrosis and cancer.

What is Gene Therapy? | FDA
Human gene therapy is the administration of genetic material to modify or manipulate the expression of a gene product or to alter the biological properties of living cells for therapeutic use.

Gene therapy: principles, challenges and use in clinical practice
Gene therapy is the transfer of genetic material to a patient to treat or potentially even cure a disease. There are various approaches of gene therapy. Most currently used gene therapy products attempt to replace the function of a defective gene with that of a healthy gene.

Gene therapy for genetic diseases: challenges and future directions
This review aims to delineate the mechanisms and outcomes of current gene therapy approaches in clinical applications across various genetic diseases affecting different body systems.